Clinical Trials Recruiting in Australia
Clinical trials tell us if a new therapy is safe and if it will help make life with PWS better.
The faster a clinical trial is completed, the sooner we know if the therapy works. You can help by taking part in clinical trials and registries. Your doctor and the study coordinator can help you decide if a trial is a good fit for you and your family.
Clinical trial resources:
Disclosure: PWFRA does not endorse or recommend any specific study, we aim to provide information about trials that people with PWS living in Australia can participate in.
PWS Clinical Trials
| Study | Type | Age | Location | Contact/Study Link | Status |
|---|---|---|---|---|---|
| Acamprosate; investigating a new target for treatment in PWS PWS FLYER Recruitment Video |
Intervention - Drug | 18-30 | Sydney RPAH | clinicaltrials.boden@sydney.edu.au or 02 8627 6048 | Recruiting |
| Tania Markovic; Gastrointestinal transit and safety of Tirzepatide in people with PWS Recruitment Video |
Intervention - Drug | adults | Sydney RPAH | fhs.devpsych@sydney.edu.au | Recruiting |
| GeneEQUAL: Co-production with people with intellectual disability to achieve more inclusive, person-centered, and respectful healthcare Study Link |
Observation (interviews) | parents/carers and/or young people with PWS (up to 28yo) | discuss with study lead | Contact: https://geneequal.com/ | Recruiting |
| Does CBD reduce severe behaviour problems in children and adolescents with intellectual disability? Recruitment Poster Recruitment Video |
Intervention (drug) | 6- 18 years | Melbourne (MCRI) and Sydney (Westmead) | clinicaltrials.boden@sydney.edu.au or 02 8627 6048 | Recruiting |
| Harmony Biosciences; TEMPO study; evaluating pitolisant for excessive daytime sleepiness in PWS Study Link |
Intervention (drug) | TBC | Qld, Sydney | opening 2025 |
PWS Registries and Biobanks
| Study | Type | Age | Location | Contact/Study Link | Status |
|---|---|---|---|---|---|
| Australian Chromosome 15 Biobank Biobank Flyer Biobank EIO |
Intervention - Biological sample collection, surveys and assessments | Any | National | diagnosis.development@mcri.edu.au | Recruiting |
| Global PWS Registry |
Observational - survey | All ages | Online | www.pwsregistry.org | Recruiting |
| Australasian Prader Willi Database | Observational - survey | 0-25 years | Online | Contact: jenny.downs@telethonkids.org.au | Recruiting |
Please forward details of additional PWS studies recruiting in Australia to info@praderwilli.org.au
Last updated: 4 November 2024
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