Clinical Trials Recruiting in Australia

Clinical trials are an important and essential step in the development of new treatments for PWS. While PWFRA does not endorse or recommend any specific study, we do seek to provide information about trials that people living in Australia can participate in.

If you are considering participating in a clinical trial please talk to your doctor and the study coordinator to find out if the trial is right for you.

Additional general information about clinical trials can be found on the Australian Clinical Trials website.

Study Type Age Location Contact/Study Link
ENGAGE study; effect of exenatide on appetite and gastric emptying (Campbell/Viardot) Drug intervention 18 Sydney
Oxytocin and the autonomic nervous system in PWS (Einfeld/Rice) Drug intervention 13-30 Sydney & Melbourne
Mindfulness-based intervention for temper outbursts (Einfeld/Rice) Behaviour intervention 13-30 Phone or web-based
PATH for PWS; understanding how PWS changes over time, and serious medical events in PWS (Zafgen/FPWR) Observational database 5+ Web-based PATH for PWS
Establishing a national platform for the provision of evidence based practice in Prader-Willi syndrome (Downs/Choong/TKI) Observational database 0-25 Nation-wide
Safety, tolerability, and effects of Livoletide (AZP-531), an unacylated ghrelin analog, on food-related behaviors in patients with Prader-Willi syndrome. Click for more information. Drug intervention 8-65 Sydney (Charles Perkins Centre) Tegan Picone 86276048 or
Experience of Adult Siblings of Individuals with Intellectual Disabilities Closing in August Click for more information. Online Survey 18 years+ Web Based Natasha Shukla at
Survey Link

Please forward details of additional PWS studies recruiting in Australia to

Last updated: 23 July 2019