Clinical Trials Recruiting in Australia

Clinical trials are an important and essential step in the development of new treatments for PWS. While PWFRA does not endorse or recommend any specific study, we do seek to provide information about trials that people living in Australia can participate in.

If you are considering participating in a clinical trial please talk to your doctor and the study coordinator to find out if the trial is right for you.

Additional general information about clinical trials can be found on the Australian Clinical Trials website.

Study Type Age Location Contact/Study Link
ENGAGE study; effect of exenatide on appetite and gastric emptying (Campbell/Viardot) Drug intervention 18 Sydney
Oxytocin and the autonomic nervous system in PWS (Einfeld/Rice) closing end April* Drug intervention 13-30 Sydney & Melbourne
Effect of Liraglutide for Weight Management in Paediatric Subjects With Prader-Willi Syndrome (NovoNordisc/RCH/Charles Perkins) Drug intervention 6-11 Sydney & Melbourne RCH: 03 9345 5570;
Charles Perkins: Ph 02 8627 1932
Mindfulness-based intervention for temper outbursts (Einfeld/Rice) Behaviour intervention 13-30 Phone or web-based
PATH for PWS; understanding how PWS changes over time, and serious medical events in PWS (Zafgen/FPWR) Observational database 5+ Web-based PATH for PWS
Establishing a national platform for the provision of evidence based practice in Prader-Willi syndrome (Downs/Choong/TKI) Observational database 0-25 Nation-wide
Safety, tolerability, and effects of Livoletide (AZP-531), an unacylated ghrelin analog, on food-related behaviors in patients with Prader-Willi syndrome. Click for more information. Double blinded, placebo controlled study 8-65 Sydney (Charles Perkins Centre) Tegan Picone 86276048 or

Please forward details of additional PWS studies recruiting in Australia to

Last updated: 11 February 2019